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Beqvez (fidanacogene elaparvovec-dzkt) – New orphan drug approval

April 29, 2024 - Pfizer announced the FDA approval of Beqvez (fidanacogene elaparvovec-dzkt), for the treatment of adults with moderate to severe hemophilia B (congenital factor IX deficiency) who currently use factor IX prophylaxis therapy, or have current or historical life-threatening hemorrhage, or have repeated, serious spontaneous bleeding episodes, and, do not have neutralizing antibodies to adeno-associated virus serotype Rh74var capsid as detected by an FDA-approved test.

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