Brineura® (cerliponase alfa) – Expanded indication
July 24, 2024, BioMarin announced the FDA approval of Brineura (cerliponase alfa), to slow the loss of ambulation in pediatric patients with neuronal ceroid lipofuscinosis type 2 (CLN2 disease), also known as tripeptidyl peptidase 1 (TPP1) deficiency.
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